Strategies to Leverage Patient Preference and Perspective to Support Development of New Drugs and Indications

For developing patient centric and patient tailored healthcare options, it is imperative to involve patient perspective from the beginning. Patients are experts in the experience of their disease or condition, especially if it is chronic. They can shed the best light on the impact that disease has on one’s life and voice what matters for them the most. Well curated, robust, and meaningful patient perspective input consistently informs the clinical and critical regulatory decision making. This information also influences Target Product Profile and proposed target label, the cornerstones of new drug and indication development.
A multitude of data generated by assessing actual patient use of marketed drugs is currently underutilized. Occasionally, this data highlights the gap existing between the treatment of multiple chronic conditions and potentially life-threatening conditions. Off-label use represents this gap reflecting extensive use in an unapproved population, often supported, or even endorsed by standard treatment practices and guidelines.
This panel will focus on strategies to leverage patient preference and perspective to support development of new drugs and indications. We will present different case studies highlighting possibilities and challenges in this area.